Biological Sciences Division
Published September 17, 2020 | Version v1
Patent Open

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES

Creators

  • 1. University of Chicago

Contributors

Patent applicant:

Description

Antisense polynucleotides and their use in pharmaceutical compositions to induce exon skipping in targeted exons of the gamma sarcoglycan gene are provided, along with methods of preventing or treating dystrophic diseases such as Limb-Girdle Muscular Dystrophy.

Files

US20200291403.pdf

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Additional details

Identifiers

Patent application number
US 202016886171 A
Patent number
US 2020/0291403 A1
Other
oai:uchicago.tind.io:9065

Dates

Patent filed
2020-05-28

UChicago Information

Division(s)
Biological Sciences Division
Department(s)
Medicine