@article{PATENT,
      recid = {7892},
      title = {Antisense Polynucleotides to Induce Exon Skipping and  Methods of Treating Dystrophies},
      number = {PATENT},
      month = {Aug},
      year = {2015},
      abstract = {Antisense polynucleotides and their use in pharmaceutical  compositions to induce exon skipping in targeted exons of  the gamma sarcoglycan gene are provided, along with methods  of preventing or treating dystrophic diseases such as  Limb-Girdle Muscular Dystrophy. One aspect the disclosure  provides an isolated antisense polynucleotide wherein the  polynucleotide specifically hybridizes to an exon target  region of a gamma sarcoglycan RNA, wherein the exon is  selected from the group consisting of exon 4 (SEQ ID NO:1),  exon 5 (SEQ ID NO: 2), exon 6 (SEQ ID NO: 3), exon 7 (SEQ  ID NO: 4) and a combination thereof. In some embodiments,  the antisense polynucleotide cannot form an RNase H  substrate, and in further embodiments the antisense  polynucleotide comprises a modified polynucleotide  backbone.},
      url = {http://knowledge.uchicago.edu/record/7892},
}